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mtm1

Early Phase Human Drug Trial to Investigate DYN101 in Participants 2 to 17 Years With Centronuclear Myopathies (DyNaMic)

A Medical Chart Review of Patients With X-Linked Myotubular Myopathy (XLMTM)

Respiratory Muscle Function in Untreated X-Linked Myotubular Myopathy (XLMTM)

Gene Transfer Clinical Study in X-Linked Myotubular Myopathy (ASPIRO)

MTM Manifesting Carrier Study

Myotubular Myopathy Event Study (MTMES)

Myotubular Myopathy Genetic Testing Study

Prospective, Longitudinal Study of the Natural History and Functional Status of Patients With Myotubular Myopathy (MTM)

Molecular and Genetic Studies of Congenital Myopathies

A Clinical Assessment Study in X-Linked Myotubular Myopathy (XLMTM) Subjects (INCEPTUS)